Sidra Medicine has marked a significant medical achievement by securing regulated access to sepiapterin for patients with Phe ...

DOHA: Sidra Medicine has announced a medical achievement by facilitating access to sepiapterin for patients with ...

Victoria Gray spent 34 years battling the debilitating pain of sickle cell disease. Then she volunteered to be the world's first "prototype" for a CRISPR therapy, based on technology invented at UC ...

GenEditBio Limited ("GenEditBio"), a clinical-stage biotechnology startup focusing on genome-editing therapeutic solutions, today announced that the U.S. Food and Drug Administration (FDA) has cleared ...

GRIN Therapeutics, Inc., a leader in the development of targeted disease-specific therapies for serious neurodevelopmental disorders, today announced that it has dosed the first patient in its global ...

As BioMendics prepares to share its progress during the 2026 J.P. Morgan Healthcare Conference and Biotech Showcase, the Ohio-based biotech is advancing what could become the first disease-modifying ...

Phase 1 proof-of-concept study of CLY-124 in Sickle Cell Disease expected in Q4 2026In vivo preclinical data assessing new compounds vs. standard of care in gold-standard, translatable myelofibrosis ...

Knowable Magazine reports 2025 faced turmoil in U.S. science amid job cuts and budget slashes, yet saw advances in gene ...

Tisento Therapeutics today announced that the global Phase 2b PRIZM study is fully enrolled. PRIZM is evaluating zagociguat – a once-daily, oral investigational medicine – as a treatment for the rare ...

Once-weekly TransCon® CNP and TransCon® hGH combination therapy showed durable growth without compromising safety or tolerability at 52 weeks– ...

Sidra Medicine introduces groundbreaking sepiapterin treatment for Phenylketonuria (PKU) patients in Qatar, becoming the ...

With these books set in and around each of the 50 states, you can tour the country without ever leaving home Notable books ...